Rare Diseases

From the National Institutes of Health
• MEDLINE Search (National Library of Medicine) - access to more than 11 million references to articles published in 4300 biomedical journals
• Rare Diseases List (Office of Rare Diseases)

Clinical Trials

• Rare Diseases Clinical Research Database (Office of Rare Diseases)

Research

• Development of Orphan Vaccines: An Industry Perspective (Centers for Disease Control and Prevention)
• From Maps to Medicine: About the Human Genome Research Project (National Human Genome Research Institute)

Treatment

• OOPD Frequently Asked Questions (Food and Drug Administration)
• Parasitic Disease Drug Service Provides "Orphan" Drugs to Treat Rare Infections (Centers for Disease Control and Prevention)
• When a Drug Is In Short Supply (Food and Drug Administration)

Directories

• Other Sources of Rare Disease/Orphan Product Information (Food and Drug Administration)
• Rare Diseases List (Office of Rare Diseases)

Law and Policy

• Orphan Drug Act and Related Law and Regulations (Food and Drug Administration)

Organizations

• Office of Rare Diseases